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PRAX

Praxis Precision Medicinesdistress 3/10 · well-funded / low risk
$311.200%today-13% from 52w high
praxismedicines.com168 employeesFounded 2015Boston, MABiotechnology
Neurology 1
Lead: focal onset seizures
Revenue
pre-revenue
Liquidity
$1448M
Runway
5.1 yrs
Shares 1y
+33%

Price & events

+2.2% over 6M
$241$299$357Jan 26Apr 26Jul 262.1Mcatalyst: PHASE3 elsunersen (2026-06-30) — click to opencatalyst: vormatrigine (2026-06-30) — click to opencatalyst: ulixacaltamide HCl (2026-04-14) — click to opencatalyst: relutrigine (2026-03-31) — click to opencatalyst: ulixacaltamide (2026-03-31) — click to opencatalyst: PHASE3 ulixacaltamide (2026-03-31) — click to openrating: Goldman Sachs: Buy (2026-07-13)rating: Needham: Buy (2026-06-29)rating: RBC Capital: Outperform (2026-06-18)rating: Baird: Outperform (2026-06-02)rating: BTIG: Buy (2026-06-02)rating: Deutsche Bank: Buy (2026-06-02)rating: HC Wainwright & Co.: Buy (2026-06-02)rating: Wedbush: Underperform (2026-06-02)
CatalystRating changeDilutionFinancingdashed = today
-0.3%
1D
+1.0%
1W
+1.9%
1M
-5.6%
3M
-0.2%
6M
+445.1%
1Y
+434.6%
2Y
+26.6%
5Y
-61.7%
All

Overview

Market Cap
$8.68B
Volume
61.87K
52 Week Range
$37.70 – $357
Total Shares
27.88M
Float Shares
24.04M
Short %
14.34%
% Held by Insiders
0.28%
% Held by Institutions
116.72%
RVOL
0.12x
Beta
2.76

Pipeline stages · 4 programs

1.0mg/kg/day PRAX-562, 1.5mg/kg/day PRAX-562
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2026-12
40 mg/day vormatrogine for 12 weeks, 30 mg/day vormatrogine for 12 weeks, 20 mg/day vormat
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2027-01
vormatrogine
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2028-05-31
PRAX-222 - Initial Dose, PRAX-222 - Initial Ascending Doses, PRAX-222 - Optional Ascending Doses, PRAX-222 - Fixed Doses
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved

Pipeline · 5 trials · 3 upcoming

ReadoutPhaseDrugIndicationEnrollStatus
2026-12
Estimated 50%
readout ~2027-02-14
Phase 31.0mg/kg/day PRAX-562, 1.5mg/kg/day PRAX-562Developmental and Epileptic Encephalopathy 1recruiting
2027-01
Estimated 50%
readout ~2027-03-17
Phase 340 mg/day vormatrogine for 12 weeks, 30 mg/day vormatrogine for 12 weeks, 20 mg/day vormatFocal Epilepsyrecruiting
2028-05-31
Estimated 50%
readout ~2028-08-14
Phase 3vormatrogineEpilepsy, Tonic-Clonic, Focal Seizure, Primary Generalized Seizureenrolling by invitation
2025-08
Phase 1/2PRAX-222 - Initial Dose, PRAX-222 - Initial Ascending Doses, PRAX-222 - Optional Ascending Doses, PRAX-222 - Fixed DosesSCN2A-DEE, Epilepsy60recruiting
2025-05-30
Phase 1PRAX-628Healthy16not yet recruiting

Upcoming readouts & decisions · our signals

1 upcoming event has our read — the sell-the-news timing call plus an experimental clinical estimate. Go Pro to see them.

Catalyst news & presentations · 21

Approved drugs (0)

  • none — clinical-stage

Capital structure — dilution & financing

Shares out: 27,878,774 · 5 offerings/1y · 0 PIPEs
🔒 Positioning — Pro
Short interest / days-to-cover, insider buys & sells.
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🔒 Top holders — Pro
Institutional ownership + quarter-over-quarter accumulation/trimming.
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Wall St ratings

strong buy · target $610 (+96% upside) · 19 analysts
  • 2026-07-13Goldman SachsBuy
  • 2026-06-29NeedhamBuy
  • 2026-06-18RBC CapitalOutperform
  • 2026-06-02BairdOutperform
  • 2026-06-02BTIGBuy
  • 2026-06-02Deutsche BankBuy

Competitors — focal onset seizures

  • XENEXenon Pharmaceuticals Inc.$6.3B · D3
  • SUPNSUPERNUS PHARMACEUTICALS, INC.$2.7B · D0
  • RAPPRapport Therapeutics, Inc.$1.9B · D3

Not financial advice. Data: ClinicalTrials.gov, SEC EDGAR, FINRA, Nasdaq, Yahoo.