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IONS

Ionis Pharmaceuticals, Inc.distress 2/10 · well-funded / low risk
$55.85+3%today-35% from 52w high
ionis.com1,402 employeesFounded 1989Carlsbad, CABiotechnology
Hematology 1
Lead: Alexander disease · target Prekallikrein
Revenue
$246M
Liquidity
$1919M
Runway
2.1 yrs
Shares 1y
+4%

Price & events

-31.7% over 6M
$52.95$69.73$86.50Jan 26Apr 26Jul 2620.4Mcatalyst: PHASE3 zilganersen (2026-04-21) — click to opencatalyst: zilganersen (2026-03-31) — click to opencatalyst: bepirovirsen (2026-03-31) — click to openrating: Guggenheim: Buy (2026-07-21)rating: Wolfe Research: Outperform → Peer Perform (2026-07-16)rating: RBC Capital: Outperform (2026-07-13)rating: HC Wainwright & Co.: Buy (2026-07-10)rating: Morgan Stanley: Overweight (2026-07-10)rating: Barclays: Overweight (2026-07-10)rating: Canaccord Genuity: Buy (2026-07-10)rating: Citigroup: Buy (2026-07-10)
CatalystRating changeDilutionFinancingdashed = today
+3.4%
1D
+2.2%
1W
-26.5%
1M
-24.6%
3M
-30.4%
6M
+31.8%
1Y
+10.7%
2Y
+46.9%
5Y
-1.6%
All

Overview

Market Cap
$9.23B
Enterprise Value
$10.38B
Volume
241.39K
52 Week Range
$40.69 – $86.50
Total Shares
165.26M
Float Shares
163.96M
Short %
13.99%
% Held by Insiders
0.61%
% Held by Institutions
107.36%
RVOL
0.07x
Beta
0.36

Pipeline stages · 9 programs

Donidalorsen
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2026-12
ION717
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2027-02
Olezarsen
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2027-03
ION582
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2027-08
ION775
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2027-09
ION440
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2027-09
Eplontersen
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2029-08
ION337
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2030-12
sapablursen
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved

Pipeline · 15 trials · 13 upcoming

ReadoutPhaseDrugIndicationEnrollStatus
2026-12
Estimated 50%
readout ~2027-02-14
Phase 3DonidalorsenHereditary Angioedemaactive not recruiting
2027-02
Estimated 50%
readout ~2027-03-18
Phase 1/2ION717Prion Diseaserecruiting
2027-03
Estimated 50%
readout ~2027-05-15
Phase 3OlezarsenSevere Hypertriglyceridemiaactive not recruiting
2027-06
Estimated 50%
readout ~2027-08-15
Phase 3OlezarsenFamilial Chylomicronemia Syndromeactive not recruiting
2027-08
Estimated 50%
readout ~2027-10-15
Phase 3ION582Angelman Syndromerecruiting
Show all 15 trials · 10 more ▾
ReadoutPhaseDrugIndicationEnrollStatus
2027-09
Estimated 50%
readout ~2027-10-16
Phase 2ION775Hypertriglyceridemia, Severe Hypertriglyceridemiarecruiting
2027-09
Estimated 50%
readout ~2027-10-16
Phase 1/2ION440Methyl CpG Binding Protein 2 (MECP2) Duplication Syndromerecruiting
2028-02
Estimated 50%
readout ~2028-04-16
Phase 3OlezarsenFamilial Chylomicronemia Syndromeactive not recruiting
2029-03
Estimated 50%
readout ~2029-04-15
Phase 1/2ION582Angelman Syndromerecruiting
2029-06
Estimated 50%
readout ~2029-08-15
Phase 3DonidalorsenHereditary Angioedema (HAE)recruiting
2029-08
Estimated 50%
readout ~2029-10-15
Phase 3EplontersenHereditary Transthyretin-Mediated Amyloid Polyneuropathyactive not recruiting
2029-08
Estimated 50%
readout ~2029-10-15
Phase 3EplontersenTransthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)enrolling by invitation
2030-12
Estimated 50%
readout ~2031-01-15
Phase 1/2ION337Dravet Syndromerecruiting
2025-06-26
Phase 2sapablursenPhlebotomy Dependent Polycythemia Vera50active not recruiting
2025-01-24
Phase 2DonidalorsenHereditary Angioedema20completed

Upcoming readouts & decisions · our signals

2 upcoming events have our read — the sell-the-news timing call plus an experimental clinical estimate. Go Pro to see them.

Catalyst news & presentations · 16

Approved drugs (2)

  • DAWNZERA (AUTOINJECTOR)DONIDALORSEN SODIUM2025 · Prescription
  • TRYNGOLZA (AUTOINJECTOR)OLEZARSEN SODIUM2024 · Prescription

Capital structure — dilution & financing

Shares out: 165,262,556 · 0 offerings/1y · 1 PIPEs
  • 2025-11-178-Kprivate_placement
  • 2025-03-128-Kmaterial_agreement
  • 2024-11-14SC 13G/Astrategic_stake
  • 2024-11-14SC 13G/Astrategic_stake
  • 2024-11-08SC 13Gstrategic_stake
  • 2024-09-10424B5offering
  • 2024-09-09424B5offering
🔒 Positioning — Pro
Short interest / days-to-cover, insider buys & sells.
Upgrade to Pro
🔒 Top holders — Pro
Institutional ownership + quarter-over-quarter accumulation/trimming.
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Wall St ratings

buy · target $93 (+66% upside) · 20 analysts
  • 2026-07-21GuggenheimBuy
  • 2026-07-16Wolfe ResearchOutperform → Peer Perform
  • 2026-07-13RBC CapitalOutperform
  • 2026-07-10HC Wainwright & Co.Buy
  • 2026-07-10Morgan StanleyOverweight
  • 2026-07-10BarclaysOverweight

Competitors — Prekallikrein

  • none identified

Not financial advice. Data: ClinicalTrials.gov, SEC EDGAR, FINRA, Nasdaq, Yahoo.