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BMRN

BioMarin Pharmaceuticaldistress 1/10 · well-funded / low risk
$57.89-1%today-10% from 52w high
biomarin.com3,221 employeesFounded 1996San Rafael, CABiotechnology
Lead: Achondroplasia
Revenue
$766M
Liquidity
$2222M
Runway
Shares 1y
+1%

Price & events

+1.2% over 6M
$49.67$56.88$64.08Jan 26Apr 26Jul 265.5Mfinancing: 8-K material_agreement (2026-04-27)financing: 8-K material_agreement (2026-02-12)catalyst: filing_acceptance (2026-02-12) — click to openrating: Citigroup: Buy (2026-07-16)rating: RBC Capital: Sector Perform (2026-07-07)rating: Canaccord Genuity: Buy (2026-05-22)rating: B of A Securities: Buy (2026-05-19)rating: Citigroup: Buy (2026-05-19)rating: HC Wainwright & Co.: Neutral (2026-05-18)rating: Canaccord Genuity: Buy (2026-05-07)rating: Evercore ISI Group: Outperform (2026-05-05)
CatalystRating changeDilutionFinancingdashed = today
-0.9%
1D
-3.5%
1W
+2.5%
1M
+7.2%
3M
+3.0%
6M
-3.0%
1Y
-31.4%
2Y
-24.9%
5Y
-32.9%
All

Overview

Market Cap
$11.19B
Enterprise Value
$10.40B
Volume
36.64K
52 Week Range
$49.67 – $64.08
Total Shares
193.28M
Float Shares
192.09M
Short %
7.22%
% Held by Insiders
0.35%
% Held by Institutions
102.13%
RVOL
0.02x
Beta
0.24

Pipeline stages · 5 programs

Vosoritide
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2026-08-01
BMN 351
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2027-04-14
Dose 1 of BMN 331, Dose 2 of BMN 331, Dose 3 of BMN 331
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2028-11
Valoctocogene roxaparvovec
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2029-04
Active BMN 111: Subcutaneous injection of recommended dose of BMN 111 based on weight-band
Preclin
Ph1
Ph2
Ph3
Filed
PDUFA
Approved
next 2038-05

Pipeline · 14 trials · 14 upcoming

ReadoutPhaseDrugIndicationEnrollStatus
2026-08-01
Estimated 50%
readout ~2026-10-15
Phase 3VosoritideHypochondroplasiaactive not recruiting
2027-03
Estimated 50%
readout ~2027-04-15
Phase 2Vosoritide InjectionNoonan Syndromerecruiting
2027-04-14
Estimated 50%
readout ~2027-05-29
Phase 1/2BMN 351Duchenne Muscular Dystrophyactive not recruiting
2027-12
Estimated 50%
readout ~2028-01-15
Phase 2BMN 111Achondroplasiaactive not recruiting
2027-12
Estimated 50%
readout ~2028-01-15
Phase 1/2BMN 307Phenylketonuria (PKU)active not recruiting
Show all 14 trials · 9 more ▾
ReadoutPhaseDrugIndicationEnrollStatus
2027-12
Estimated 50%
readout ~2028-01-15
Phase 2vosoritideAchondroplasiaactive not recruiting
2028-06-30
Estimated 50%
readout ~2028-08-14
Phase 2VosoritideHypochondroplasiarecruiting
2028-11
Estimated 50%
readout ~2028-12-16
Phase 1/2Dose 1 of BMN 331, Dose 2 of BMN 331, Dose 3 of BMN 331Hereditary Angioedema, HAEactive not recruiting
2029-04
Estimated 50%
readout ~2029-05-16
Phase 1/2Valoctocogene roxaparvovecHemophilia A With Inhibitor, Hemophilia A With Anti Factor VIIIactive not recruiting
2029-06
Estimated 50%
readout ~2029-08-15
Phase 2/3BMN 333, Vosoritide Injection [Voxzogo]Achondroplasiarecruiting
2031-06
Estimated 50%
readout ~2031-08-15
Phase 3BMN 111Achondroplasiaactive not recruiting
2031-12
Estimated 50%
readout ~2032-01-15
Phase 2BMN 351Duchenne Muscular Dystrophy (DMD)enrolling by invitation
2038-05
Estimated 50%
readout ~2038-06-15
Phase 2Active BMN 111: Subcutaneous injection of recommended dose of BMN 111 based on weight-bandAchondroplasiaactive not recruiting
2040-12
Estimated 50%
readout ~2041-02-14
Phase 3VosoritideHypochondroplasiaenrolling by invitation

Catalyst news & presentations · 7

Approved drugs (8)

  • VOXZOGOVOSORITIDE2021 · Prescription
  • PALYNZIQPEGVALIASE-PQPZ2018 · Prescription
  • BRINEURACERLIPONASE ALFA2017 · Prescription
  • VIMIZIMELOSULFASE ALFA2014 · Prescription
  • KUVANSAPROPTERIN DIHYDROCHLORIDE2013 · Prescription
  • KUVANSAPROPTERIN DIHYDROCHLORIDE2007 · Prescription
  • NAGLAZYMEGALSULFASE2005 · Prescription
  • ALDURAZYMELARONIDASE2003 · Prescription

Capital structure — dilution & financing

Shares out: 193,284,438 · 0 offerings/1y · 0 PIPEs
  • 2026-04-278-Kmaterial_agreement
  • 2026-02-128-Kmaterial_agreement
  • 2025-12-198-Kmaterial_agreement
  • 2025-05-168-Kmaterial_agreement
  • 2024-09-30SC 13Gstrategic_stake
  • 2024-09-048-Kmaterial_agreement
  • 2024-07-10SC 13G/Astrategic_stake
🔒 Positioning — Pro
Short interest / days-to-cover, insider buys & sells.
Upgrade to Pro
🔒 Top holders — Pro
Institutional ownership + quarter-over-quarter accumulation/trimming.
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Wall St ratings

buy · target $88 (+52% upside) · 25 analysts
  • 2026-07-16CitigroupBuy
  • 2026-07-07RBC CapitalSector Perform
  • 2026-05-22Canaccord GenuityBuy
  • 2026-05-19B of A SecuritiesBuy
  • 2026-05-19CitigroupBuy
  • 2026-05-18HC Wainwright & Co.Neutral

Competitors — Achondroplasia

  • BBIOBridgeBio Pharma, Inc.$16.1B · D1
  • ASNDAscendis Pharma A/S$15.6B · D0
  • TYRATyra Biosciences, Inc.$1.8B · D3

Not financial advice. Data: ClinicalTrials.gov, SEC EDGAR, FINRA, Nasdaq, Yahoo.